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Optimized Artificial miRNAs Delivered by rAAV9 Dramatically Improve Survival, Respiratory and Motor Functions of SOD1(G93A)-ALS Mice

2024.05.10

Optimized Artificial miRNAs Delivered by rAAV9 Dramatically Improve Survival, Respiratory and Motor Functions of SOD1(G93A)-ALS Mice

Identification of Artificial microRNAs Targeting C9orf72 Sense and Antisense Transcripts for ALS treatment

2024.05.10

Identification of Artificial microRNAs Targeting C9orf72 Sense and Antisense Transcripts for ALS treatment

Directed Evolution of Rationally-Engineered AAV Capsid Variants with Enhanced Central Nervous System (CNS) Tropism Following Systematic Administration

2024.05.09

Directed Evolution of Rationally-Engineered AAV Capsid Variants with Enhanced Central Nervous System (CNS) Tropism Following Systematic Administration

Discovering rationally-engineered AAV5-derived capsid variants for superior CNS tropism and peripheral tissue de-targeting in non-human primate via systemic administration

2024.05.08

Discovering rationally-engineered AAV5-derived capsid variants for superior CNS tropism and peripheral tissue de-targeting in non-human primate via systemic administration

A Selective M4 Receptor Positive Allosteric Modulator for the Treatment of Schizophrenia

2023.11.13

A Selective M4 Receptor Positive Allosteric Modulator for the Treatment of Schizophrenia

Optimized Artificial miRNAs Delivered by AAV9 Dramatically Improve Survival, Respiratory and Motor Functions of SOD1G93A-ALS Mice

2023.10.25

Optimized Artificial miRNAs Delivered by AAV9 Dramatically Improve Survival, Respiratory and Motor Functions of SOD1G93A-ALS Mice

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